Fighting rare diseases
In the UK, there are thousands of children living with a rare and life-limiting disease for which there is no cure.
Children like Danny who has the rare disease, Hunter syndrome. Danny’s family are painfully aware that time with their youngest son will be cruelly cut short by this disease.
“We will lose our beautiful boy to Hunter syndrome,” says mum Sally. “But any new hope is worth fighting for. So that families in the future don’t have to feel that the bottom is dropping out of their world.”
Help fund vital research – together we can bring hope to families fighting rare and incurable diseases.
Other appeals
Searching for a new treatment
Help fund an urgently needed piece of research that could lead to a new treatment to improve the outlook for children fighting Vici syndrome - a devastating rare disease that can severely shorten children’s lives, with many not living beyond their fifth birthday.
Fighting premature birth
Over 1,000 babies die each year in the UK due to premature birth. Globally, it’s the biggest killer of children under 5.
Join the fight for babies born too soon. Together we will find the answers.
Life-saving new treatment for babies
Without a lung transplant, less than one in five children born with lung surfactant deficiency, a rare lung condition, will live to celebrate their fifth birthday. With your help we can support research that could change this and help save babies' lives.